Neurocritical Care News

Topline results from the phase 3 SAPPHIRE clinical trial showed that an investigational muscle-targeted therapy improved motor function in patients with spinal muscular atrophy compared with placebo as early as week 8.

Boston Children’s Hospital has been named the best hospital in the country for pediatric neurology and neurosurgery, according to a press release from U.S. News & World Report.

The FDA has granted investigational device exemption to a clinical-stage health care firm for its proprietary neuroimmune modulation platform for individuals with relapsing-remitting MS, according to the manufacturer.

Interim results from the COMMAND study evaluating the safety and efficacy of the Synchron brain-computer interface device found no serious adverse device-related events at 12 months, the company announced.

ORLANDO, Fla. — An analysis of a large cohort of individuals enrolled in a continuous, multinational survey found no clear associations between brain and heart health and pet ownership, according to a poster.

ORLANDO, Fla. — A pilot study of direct spinal cord stimulation showed promise for improving motor function in a small cohort of individuals with gait freezing in Parkinson’s disease, according to a presenter.

ORLANDO, Fla. — Managing dystonic cerebral palsy in younger populations presents unique challenges, which may be addressed with direct cerebellar implantation of a deep brain stimulation device, according to a presenter.

The FDA has approved Aqneursa as an oral treatment for neurological symptoms associated with Niemann-Pick disease type C, a rare genetic disease, in adults and children weighing at least 15 kg, according to a press release.

ORLANDO, Fla. — An algorithm for standardizing myasthenia gravis diagnosis during telehealth is feasible, but it requires additional testing and validation, according to researchers.

ORLANDO, Fla. — Cell-based therapies and enzyme inhibitors currently in development are likely to become the next-generation treatments for ambulatory and non-ambulatory forms of muscular dystrophy, according to a speaker.