Huntington's Disease Awareness

Kathryn P. L. Moore, MD, MSc

Moore reports no relevant financial disclosures.
February 22, 2024
1 min watch
Save

VIDEO: ‘A lot in the pipeline’ for Huntington’s disease

Transcript

Editor’s note: This is an automatically generated transcript, which has been slightly edited for clarity. Please notify editor@healio.com if there are concerns regarding accuracy of the transcription.

So there's a lot in the pipeline as opposed to years past where pharmaceutical companies were sort of hands off when it came to Huntington's disease. There's a lot of excitement in the field, particularly because we know the gene that causes Huntington's disease. So there's a number of approaches currently under investigation to actively target that cause of Huntington's disease. So we know the Huntington protein is necessary for embryonic development, so we can't completely knock out Huntington's. But there is a number of approaches whether directly injecting medication into the brain, the spinal fluid or even oral medications that are being explored to help control the abnormal Huntington gene, RNA or protein.