Sickle Cell Disease
Lung ultrasonography ‘rapid, sensitive and safe’ in detecting acute chest syndrome
Using lung ultrasonography to identify acute chest syndrome in patients with sickle cell disease resulted in favorable diagnostic accuracy, sensitivity and specificity, according to results published in CHEST.
ASH recap: ‘Transformative’ advance in sickle cell disease, ‘breakthrough’ in AML and ALL
Patients with sickle cell disease using disease-modifying therapies more, but not enough
Nearly three-quarters of individuals with sickle cell disease are not using disease-modifying therapies in their treatment, according to a study published in JAMA Network Open.
Haploidentical bone marrow transplant provides ‘higher access’ to sickle cell disease cure
Reduced-intensity haploidentical-bone marrow transplant showed durable donor engraftment at 2-years follow-up with low mortality among adults with severe sickle cell disease, according to study results.
Former ASH president honored for dedication to improving care of underserved populations
Alexis Thompson, MD, MPH, is an optimist.
Guideline-directed care may reduce sickle cell-related cerebrovascular disease
SAN DIEGO — Guideline-directed use of hydroxyurea may reduce cerebrovascular disease among individuals with sickle cell disease, according to single-center study results.
Patients with sickle cell disease feel ‘ignored’ during visits with health care providers
SAN DIEGO — Social media listening can provide clinicians with a novel and valuable method of identifying challenges and unmet needs of patients with sickle cell disease that they otherwise might not share during medical visits.
Lovo-cel gene therapy ‘transformative’ for sickle cell disease
SAN DIEGO — One-time treatment with lovotibeglogene autotemcel gene therapy conferred “transformative” benefit to patients with sickle cell disease, according to a presenter at ASH Annual Meeting and Exposition.
FDA approves first gene therapies for sickle cell disease
The FDA approved the first two cell-based gene therapies for treatment of sickle cell disease.
Those affected by sickle cell disease willing to accept gene therapy risks
Individuals with severe sickle cell disease showed willingness to accept the risks associated with emerging gene therapy treatments, according to survey results published in Blood Advances.