Sickle Cell Disease
Sickle Cell Data Collection program to continue key initiatives with $2.5M funding increase
Sickle cell disease affects about 100,000 people in the United States, but the exact incidence is unknown and rates vary from state to state.
Corticosteroids may increase risk for hospitalization for sickle cell disease pain crises
Exposure to systemic corticosteroids appeared to increase risk for hospitalization for vaso-occlusive episodes among patients with sickle cell disease, according to a French study published in Blood.
Organ dysfunction rare among children who underwent HSCT for sickle cell disease
SALT LAKE CITY — Prevalence of organ dysfunction appeared low among pediatric patients who underwent hematopoietic stem cell transplantation for sickle cell disease, according to retrospective study results.
Sickle cell disease increases risk for transplant-associated thrombotic microangiopathy
SALT LAKE CITY — Sickle cell disease increased risk for transplant-associated thrombotic microangiopathy among children who underwent hematopoietic stem cell transplantation, according to study results.
Many male AYAs with sickle cell disease unaware of disease-related fertility issues
Most male adolescents and young adults with sickle cell disease reported a desire to have children later in life but few knew of disease-related fertility issues, according to study results published in Blood Advances.
UCSF researchers hope to cure sickle cell disease through CRISPR gene editing
With the aid of $17 million in grant funding, UCSF Benioff Children’s Hospital Oakland will initiate a 4-year trial evaluating CRISPR/Cas9 gene editing as a potential cure for sickle cell disease.
Music therapy helps patients with sickle cell disease cope with pain
According to one patient undergoing treatment for sickle cell disease at University Hospitals Connor Whole Health, pain associated with the disease “feels like someone’s constantly stabbing you, but you’re not dying.”
ASH president advises that early-career women be persistent, ‘show up and be in the room’
Jane N. Winter, MD, the current American Society of Hematology president, advised that it’s essential to be persistent with your goals and choose mentors wisely during the early years of a medical career.
Sickle cell disease specialist named genetic medicine director at Johns Hopkins
Ambroise Wonkam, MD, PhD, DMedSc, has been appointed director of the department of genetic medicine at Johns Hopkins Medicine.
Gene therapy shows promise as potential cure for sickle cell disease
LentiGlobin led to a reduction in hemolysis and complete resolution of severe vaso-occlusive events among a small cohort of patients with sickle cell disease, according to study results published in The New England Journal of Medicine.