Sickle Cell Disease
ASH recap: New regimens for blood cancers; gene therapy equitable for sickle cell disease
This year’s ASH Annual Meeting and Exposition spotlighted practice-changing research in malignant and benign hematology.
FDA lifts partial clinical hold on studies of gene therapy for sickle cell disease
The FDA lifted its partial clinical hold on bluebird bio’s sickle cell disease studies evaluating lovotibeglogene autotemcel among patients aged younger than 18 years, according to the agent’s manufacturer.
National registry may reduce mortality among alloimmunized people with sickle cell disease
A nationwide red blood cell alloantibody exchange could reduce mortality among alloimmunized individuals with sickle cell disease, according to study results presented at ASH Annual Meeting and Exposition.
Gene therapy may be equitable therapeutic option for sickle cell disease in US
Gene therapy could represent an equitable therapeutic strategy for sickle cell disease in the United States, according to study results presented at ASH Annual Meeting and Exposition.
Children not getting ‘essential’ sickle cell treatment in sub-Saharan Africa
Children with sickle cell disease living in sub-Saharan Africa do not have access to an “essential” treatment, experts wrote this week in The New England Journal of Medicine.
Lifetime medical costs of sickle cell disease total $1.7 million
Privately insured individuals with sickle cell disease spend about $1.7 million on disease-related medical expenses during their lifetime, according to study results published in Blood Advances.
VIDEO: Perform annual dilated fundus exams on all patients with sickle cell disease
CHICAGO – Patients with sickle cell disease should be examined yearly, with a dilated fundus exam and macular OCT, Daniel Epshtein, OD, FAAO, said at Optometry’s Meeting.
Top in hem/onc: Therapy for sickle cell disease; social media use among oncologists
New research suggests that an investigational CRISPR/Cas9 gene-edited cell therapy may offer a functional cure for beta-thalassemia and sickle cell disease.
Sickle cell disease: Expanded surveillance, new treatments and the power of music therapy
World Sickle Cell Day is observed each year on June 19.
Exa-cel may offer functional cure for beta-thalassemia, sickle cell disease, new data show
An investigational CRISPR/Cas9 gene-edited cell therapy demonstrated significant, durable efficacy among patients with transfusion-dependent beta-thalassemia and sickle cell disease, according to study results.