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Gene Therapy
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January 05, 2024
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Survey: Halting neurodegeneration chief concern in Huntington’s disease
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January 05, 2024
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CMS issues permanent J-code for Vyjuvek
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January 02, 2024
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Vyjuvek receives orphan drug designation in Japan for epidermolysis bullosa
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December 30, 2023
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ASH recap: ‘Transformative’ advance in sickle cell disease, ‘breakthrough’ in AML and ALL
News
December 28, 2023
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AAV-based gene therapies hold promise for treating CNS conditions
News
December 22, 2023
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Positive interim data shown in phase 1/2 trials of Huntington’s disease therapy
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December 19, 2023
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Future of epilepsy treatment depends on overcoming obstacles to gene-targeting therapy
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December 18, 2023
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VIDEO: Updated data on hemophilia A gene therapies presented at ASH
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December 18, 2023
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VIDEO: Factor VIII variant shows ‘unclear biochemical mechanism for improved function’
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December 18, 2023
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