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Gene Therapy
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November 29, 2022
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Eikonoklastes, Forge announce partnership to develop ALS gene therapy
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November 25, 2022
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VIDEO: Several options for gene therapy in treatment of geographic atrophy
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November 22, 2022
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FDA approves Hemgenix as first gene therapy for treatment of hemophilia B
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November 21, 2022
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Phase 2/3 study of gene therapy for young children with MPS IIIA yields mixed results
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November 17, 2022
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VIDEO: Gene therapy shows growing promise in treatment of retinal diseases
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October 25, 2022
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VIDEO: Gene therapy potential treatment target for Duchenne muscular dystrophy
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October 24, 2022
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VIDEO: Gene therapy shows positive safety, tolerability results for geographic atrophy
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October 02, 2022
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VIDEO: Gene therapy for X-linked retinitis pigmentosa shows positive safety, efficacy data
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October 01, 2022
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VIDEO: Opus Genetics CEO discusses IND application for retinal degeneration gene therapy
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September 19, 2022
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