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Non-Small Cell Lung Cancer
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Precision and Immune-Based Therapies

Edward S. Kim, MD, MBA, FACP, FASCO

Free clinical reference tool that includes treatment options; diagnosis information; guidelines; and more.

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December 21, 2023
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Positive data in study of drug for Duchenne muscular dystrophy with exon 44 skipping

Positive data in study of drug for Duchenne muscular dystrophy with exon 44 skipping

Avidity Biosciences Inc. has announced positive data in healthy volunteers from its ongoing phase 1/2 clinical trial of a proprietary monoclonal antibody to treat Duchenne muscular dystrophy mutations amenable to exon 44 skipping.

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April 28, 2023
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FDA grants fast track designation to exon-skipping Duchenne muscular dystrophy therapy

FDA grants fast track designation to exon-skipping Duchenne muscular dystrophy therapy

The FDA has granted fast track designation to AOC 1044 for the treatment of Duchenne muscular dystrophy in people with mutations amenable to exon 44 skipping, Avidity Biosciences announced in a press release.