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Etranacogene Dezaparvovec

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February 22, 2023
3 min read
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Gene therapy ‘clearly superior’ for patients with hemophilia B

Etranacogene dezaparvovec conferred superior bleed control for adults with moderate or severe hemophilia B compared with standard factor IX prophylaxis, according to results of the phase 3 HOPE-B study.

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December 08, 2020
4 min read
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Single-dose gene therapy ‘pretty transformative’ for patients with hemophilia B

The gene therapy etranacogene dezaparvovec conferred a substantial decrease in bleeding events among patients with moderate or severe hemophilia B, according to preliminary data presented at the virtual ASH Annual Meeting and Exposition.