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Antitrypsin Deficiency-Associated Liver Disease

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July 22, 2024
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Fazirsiran lowers serum, liver concentrations of Z-AAT in alpha-1 antitrypsin deficiency

Fazirsiran lowers serum, liver concentrations of Z-AAT in alpha-1 antitrypsin deficiency

In a dose-dependent manner, fazirsiran reduced serum and liver concentrations of Z-AAT and also improved histological measures in patients with homozygous ZZ alpha-1 antitrypsin deficiency-associated liver disease, according to data.