Pediatric Neurology News

Sexual and gender minority health care in child neurology is “such an important topic that just hasn’t gotten enough attention,” according to Ariel Maia Lyons-Warren, MD, PhD.

Ariel Maia Lyons-Warren, MD, PhD, an instructor of child neurology at Baylor College of Medicine and Texas Children’s Hospital, discusses what stood out to her at the Child Neurology Society annual meeting in Vancouver.

The FDA has approved a 40 mg/mL oral suspension of Agamree to treat Duchenne muscular dystrophy in patients aged 2 years and older, according to a release from the manufacturer.

Ecopipam, a novel investigational compound for central nervous system disorders significantly reduced symptoms of Tourette syndrome in a cohort of pediatric patients, according to the manufacturer.

Robert C. Stowe, MD, an instructor of neurology at Boston Children’s Hospital and Harvard Medical School, discusses highlights from the Child Neurology Society annual meeting in this Healio video.

Hospitalized patients with multisystem inflammatory syndrome in children — or MIS-C —are far more likely to experience shock than those hospitalized with Kawasaki disease, according to a study.

Genentech has announced positive results from its primary analysis of an ongoing study assessing safety and efficacy of Evrysdi in babies with pre-symptomatic spinal muscular atrophy.

A Bay Area biotech company announced the FDA has lifted the partial clinical hold on EryDel SpA’s investigational new drug application for EryDex to treat ataxia-telangiectasia, a rare pediatric neurological disorder.

Constipation is a relatively common problem in pediatric practice, with reported prevalence rates between 1% and 30%, as well as the chief complaint in 3% to 5% of visits to pediatric outpatient clinics. Because most constipation cases can be remedied through recommended over-the-counter laxatives, constipation is rarely a cause for severe worry among parents.

Expanding newborn screening to identify genes associated with an increased risk for neurodevelopmental disorders could exacerbate disparities, among other drawbacks, experts wrote in Pediatrics.