Pediatric Neurology News

The FDA has approved an abbreviated new drug application for a generic version of Emflaza to treat Duchenne muscular dystrophy, according to the manufacturer.

Newly released data from the open-label extension of the FIREFISH study confirmed sustained safety and efficacy of Evrysdi in children with type 1 spinal muscular atrophy over 5 years.

The FDA has selected an investigational AAV9 gene therapy for Rett syndrome to participate in a pilot program created to provide a boost to novel drug development for rare diseases, according to a release from the manufacturer.

Higher fluoride levels in pregnancy were linked to increased odds of offspring exhibiting neurobehavioral issues by age , according to research published in JAMA Network Open.

DENVER — Primary generalized tonic-clonic seizures present unique challenges to adolescents diagnosed with the condition, Sunita Misra, MD, PhD, said in this Healio video at the American Academy of Neurology annual meeting.

According to statistics reported in a recent release from Sutter Health, up to 15% of strokes are suffered by individuals aged younger than 45 years, with incidence rising.

Persistent shorter sleep durations during childhood were associated with a greater risk of psychosis disorder and psychotic episodes during early adulthood, a study in JAMA Psychiatry showed.

DENVER — Treatment with a novel therapeutic led to clinically significant improvement in cognition for young persons with Angelman syndrome, Kemi Olugemo, MD, FAAN, said in this Healio video at the American Academy of Neurology annual meeting.

The FDA has granted orphan drug designation to a microbiome-modifying biologic to treat Angelman syndrome, according to the manufacturer.

DENVER — Lidocaine injection in the occipital region for young persons with acute migraine significantly increased pain relief compared with saline injections, according to research presented at the American Academy of Neurology annual meeting.